Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...

Having two copies of the MTHFR gene mutation may raise your risk for certain health conditions, though more research is needed. You may have the mutation and not find out unless you undergo ...

Building a gene editor took months. With CRISPR even high-schoolers can get hold of editing systems in the time it takes to order RNA sequences online and have them shipped by FedEx. In a short ...

Jace, 6, was born with a rare and aggressive eye condition An experimental trial of gene therapy has helped four toddlers - born with one of the most severe forms of childhood blindness - gain ...

Pfizer’s decision to halt further marketing of Beqvez is further sign of the sparse patient interest in gene therapies for the bleeding condition. Rapid scientific advances have put the gene therapy ...

A new study links a particular gene to the ancient origins of spoken language, proposing that a protein variant found only in humans may have helped us communicate in a novel way. Speech allowed us to ...

A new study suggests that the NOVA1 gene may have been a key player in the evolution of human language. By Carl Zimmer Scientists have long struggled to understand how human language evolved.

Mice carrying a gene variant present in nearly every human on Earth — but not in extinct relatives including Neanderthals — produce more-complex chirps than normal rodents do 1. The finding ...

Researchers developed a new gene-editing strategy that dramatically boosts the effectiveness of gene therapies in the liver, a breakthrough that could lead to new treatments for about 700 genetic ...